Director, Rare Disease Specialist

1 week ago


Boston, Massachusetts, United States X4 Pharmaceuticals Full time
Job Summary

We are seeking a highly motivated and experienced Director of Rare Disease Management to join our team at X4 Pharmaceuticals. As a key member of our commercial organization, you will be responsible for driving patient identification and access to our innovative treatments in the Central Plains region.

Key Responsibilities
  • Develop and execute territory-level business plans to drive patient identification and access to our treatments
  • Build and maintain relationships with healthcare professionals and office staff to maximize their time and optimize access to our treatments
  • Collaborate with internal and external stakeholders to ensure seamless execution of commercial strategies
  • Drive market development and physician education to increase awareness and adoption of our treatments
  • Report territory-level market dynamics and trends to inform business decisions
Requirements
  • Bachelor's degree required
  • 7-10+ years of experience in biotech, ultra-rare diseases in the U.S.
  • Rare/orphan disease experience within the last 10 years in Immunology and/or benign hematology
  • U.S. launch experience required, along with demonstrated successes
  • Miscellaneous J-code product launch experience required, including a working knowledge of government and commercial payers
  • Understanding and experience working with HUB patient services required
  • Hospital/institution knowledge and expertise with pharmacy formulary processes in academic settings
  • Experience driving, leading, and delivering upon territory-level cross-functional business planning
  • Familiarity with relevant legal and regulatory environment in biotech/pharmaceutical industry
  • Understanding of charitable access and specialty channel distribution is preferred
  • Experience supporting oral biologic therapy preferred
  • Effective communication and listening skills
  • Effective at managing complex individualized cases in a compliant manner
What We Offer
  • A team that values grit and passion for innovative science
  • The opportunity to leverage your knowledge of Rare Disease to support our innovative science and make a major impact on our mission
  • A collegial environment with a team-based approach, where our mission drives our values, behaviors, and creativity


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